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Gangliosidoses, GM2

Showing 1 - 25 of 7,725

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Infantile GM2 Gangliosidosis (Disorder) Trial in Kingston (TSHA-101)

Active, not recruiting
  • Infantile GM2 Gangliosidosis (Disorder)
  • TSHA-101
  • Kingston, Ontario, Canada
    Queen's University/Kingston Health Sciences Centre
Sep 12, 2022

GM2 Gangliosidosis, Niemann-Pick Disease, Type C Trial in Curitiba, Porto Alegre, Rio De Janeiro (AZ-3102 (Dose 1), Placebo,

Not yet recruiting
  • GM2 Gangliosidosis
  • Niemann-Pick Disease, Type C
  • AZ-3102 (Dose 1)
  • +2 more
  • Curitiba, Brazil
  • +2 more
Feb 24, 2023

GM1 and GM2 Gangliosidosis PROspective Neurological Disease

Recruiting
  • GM1 Gangliosidosis
  • +2 more
    • Oakland, California
    • +12 more
    Nov 16, 2022

    GM2 Gangliosidosis, Supportive Care Trial in Kashan, Mashhad, Tehran (Miglustat)

    Recruiting
    • GM2 Gangliosidosis
    • Supportive Care
    • Kashan, Isfahan, Iran, Islamic Republic of
    • +2 more
    Oct 23, 2022

    A Natural History Study of the Gangliosidoses

    Recruiting
    • Tay-Sachs Disease
    • +4 more
      • Minneapolis, Minnesota
        University of Minnesota - Pediatric Genetics and Metabolism
      Feb 28, 2022

      GM1 Gangliosidoses, GM2 Gangliosidoses, Tay-Sachs Disease Trial in Minneapolis (miglustat, Ketogenic Diet)

      Terminated
      • GM1 Gangliosidoses
      • +3 more
      • Minneapolis, Minnesota
        University of Minnesota
      Mar 18, 2021

      Gangliosidoses, GM1 Gangliosidosis, Morquio B Disease Trial in Hochheim

      Recruiting
      • Gangliosidoses
      • +8 more
        • Hochheim, HE, Germany
          SphinCS Lyso gemeinnützige UG (haftungsbeschränkt)
        Nov 5, 2020

        Lysosomal Diseases, Gangliosidosis, GM1 Trial run by the NHGRI (biological, drug, diagnostic test, other, procedure, behavioral)

        Recruiting
        • Lysosomal Diseases
        • +2 more
        • AAV9-GLB1
        • +20 more
        • Bethesda, Maryland
          National Institutes of Health Clinical Center
        Jan 19, 2023

        GM2 Gangliosidosis Trial in Boston

        Recruiting
        • GM2 Gangliosidosis
          • Boston, Massachusetts
            Massachusetts General Hospital
          Sep 8, 2020

          GM1 Gangliosidosis, GM1 Gangliosidosis, Type I, GM1 Gangliosidosis, Type 2 Trial in Worldwide (PBGM01)

          Recruiting
          • GM1 Gangliosidosis
          • +3 more
          • PBGM01
          • Oakland, California
          • +9 more
          Mar 10, 2022

          Biomarker for Gangliosidosis: BioGM1/BioGM2 (BioGM1/GM2)

          Active, not recruiting
          • Hepato-splenomegaly
          • +3 more
            • Cairo, Egypt
            • +4 more
            May 12, 2021

            Infantile and Juvenile GM1 Gangliosidosis (GM1) Patients

            Recruiting
            • GM1 Gangliosidosis
              • Oakland, California
              • +5 more
              Feb 2, 2023

              ScreenPlus: A Comprehensive, Flexible, Multi-disorder Newborn

              Enrolling by invitation
              • Acid Sphingomyelinase Deficiency
              • +13 more
              • Confirmatory Testing
              • Bronx, New York
              • +9 more
              May 9, 2022

              Interviews and Video Capture in Patients With GM1 Gangliosidosis

              Recruiting
              • GM1 Gangliosidosis
              • Natural history
              • Plymouth, Massachusetts
                Casimir Trials
              Aug 23, 2021

              GM1 Gangliosidosis Trial in Orange, Paris, Manchester (LYS-GM101)

              Recruiting
              • GM1 Gangliosidosis
              • LYS-GM101
              • Orange, California
              • +2 more
              Jun 30, 2021

              Brain Metastases, Radiotherapy Side Effect, Cognitive Impairment Trial in Guangzhou (Monosialotetrahexosyl ganglioside (GM1),

              Recruiting
              • Brain Metastases
              • +4 more
              • Monosialotetrahexosyl ganglioside (GM1)
              • Control
              • Guangzhou, Guangdong, China
                Sun Yat-sen University Cancer Center
              Nov 3, 2021

              The Natural History of Metachromatic Leukodystrophy

              Recruiting
              • MLD
              • +26 more
              • Palliative Care
              • Hematopoetic Stem Cell Transplantation
              • Pittsburgh, Pennsylvania
                The Program for the Study of Neurodevelopment in Rare Disorders,
              Nov 2, 2021

              Psoriasis Vulgaris, Fractional CO2 Laser Trial in Assiut (Topical Ointment containing Calcipotriol 0.05 mg/gm and Betamethasone

              Completed
              • Psoriasis Vulgaris
              • Fractional CO2 Laser
              • Topical Ointment containing Calcipotriol 0.05 mg/gm and Betamethasone dipropionate 0.5 mg/gm
              • Fractional carbon dioxide (CO2) laser
              • Assiut, Egypt
                Assiut University
              Aug 23, 2023

              ICU Acquired Weakness Trial (patients who will receive 2 gm protein/kg/day will be evaluated by ultrasound for diaphragmatic

              Not yet recruiting
              • ICU Acquired Weakness
              • patients who will receive 2 gm protein/kg/day will be evaluated by ultrasound for diaphragmatic function and quadriceps muscle thickness
              • (no location specified)
              Sep 13, 2023

              DLBCL Trial in Suzhou (Chidamide, Azacitidine, obinutuzumab)

              Recruiting
              • Diffuse Large B-Cell Lymphoma
              • Suzhou, Jiangsu, China
                the First Affiliated Hospital of Soochow University
              Apr 10, 2023

              NSCLC, Carcinoma Breast Trial in Suzhou (Vinorelbine, Radiotherapy, PD-1/PD-L1 inhibitor)

              Not yet recruiting
              • Carcinoma, Non-Small-Cell Lung
              • Carcinoma Breast
              • Suzhou, China
                Second Affiliated Hospital of Soochow University
              Oct 29, 2022

              HER2-positive Breast Cancer, Stage III Ovarian Epithelial Cancer, Stage III Ovarian Germ Cell Tumor Trial in Seattle

              Active, not recruiting
              • HER2-positive Breast Cancer
              • +8 more
              • pNGVL3-hICD vaccine
              • +6 more
              • Seattle, Washington
                Fred Hutchinson Cancer Research Center/University of Washington
              Nov 1, 2022

              Recurrent Osteosarcoma Trial in Los Angeles, New York, Houston (humanized anti-GD2 antibody, GM-CSF)

              Recruiting
              • Recurrent Osteosarcoma
              • humanized anti-GD2 antibody
              • GM-CSF
              • Los Angeles, California
              • +2 more
              Dec 22, 2022

              Melanoma Trial in Beijing (OH2 injection, HX008 injection)

              Recruiting
              • Melanoma
              • OH2 injection
              • HX008 injection
              • Beijing, Beijing, China
                Peking University Cancer Hospital
              Jan 28, 2023

              Neuroblastoma Trial in New York (anti-GD2 murine IgG3 mAb 3F8)

              Completed
              • Neuroblastoma
              • anti-GD2 murine IgG3 monoclonal antibody 3F8
              • New York, New York
                Memorial Sloan-Kettering Cancer Center
              Apr 21, 2022